Sebelipase alfa

Grey

Brand Name(s):KANUMA

Indication:Lysosomal acid lipase (LAL) deficiency – long term enzyme replacement therapy (ERT)

Rationale:1,2,3

Considered:Sep-15

Review Date:Jan-26

Comments:
Sebelipase alfa is not recommended for treating LAL deficiency in children or adults. Information can be found at: https://www.nice.org.uk/guidance/gid-lysosomalacidlipasedeficiencysebelipasealfaid737/documents/final-evaluation-determination-document